Gene Therapy

Duchenne UK Gene Therapy Industry Workshop - March 2022


Description
Recordings of talks from the Duchenne UK gene therapy industry workshop, discussing the current and future state of DMD gene therapy trials. Workshop took place on 4th March 2022.
Content
  • 1) Patient Perspective - Emily Reuben & Alex Johnson, Duchenne UK
  • 2) DMD Hub Institutional Readiness - Emma Heslop, Newcastle University
  • 3) Clinical Perspective - Dr Michela Guglieri, Newcastle University
  • 4) Regulatory Perspective - John Johnstone, MHRA
  • 5) HTA Perspective - Ron Akehurst, BresMed and University of Sheffield
  • 6) Commissioner Perspective - Fiona Marley, NHS England
  • 7) Speaker Panel Q&A
Completion rules
  • All units must be completed